Oct. 25, 2012
TOPIC: Advocacy, Industry, Medical, Patients & Members, Research

The Word That Best Describes This Week’s Rare Diseases/Orphan Products Summit

Posted at October 25, 2012 7:58 pm by Wayne Pines

The single word that describes this week’s Rare Disease/Orphan Product meeting is read more >

TAGS: , , , , , , , , ,
Oct. 24, 2012
TOPIC: Advocacy, Industry, Medical, Patients & Members, Research

Reduced Investment in Biomedical Innovation is Potentially Devastating for Patients

Posted at October 24, 2012 3:38 pm by Mary Dunkle

2011 and 2012 have been good years but the rate of innovation in drug development is anything but healthy, a venture investor focusing on the life sciences said yesterday at the U.S. Conference on Rare Diseases and Orphan Products underway this week in Washington DC.  read more >

TAGS: , , ,
Oct. 23, 2012
TOPIC: Advocacy, Featured News, Industry, Medical, Patients & Members, Research

Rare Disease Regulatory Pathway is Becoming the New Norm

Posted at October 23, 2012 2:11 pm by Mary Dunkle

The regulatory pathway that we have learned from rare diseases is now becoming the paradigm in general, FDA Deputy Commissioner Stephen P. Spielberg, MD, PhD, said this morning in the opening session of Day 2 of the U.S. Conference on Rare Diseases and Orphan Products.

read more >

TAGS: , ,
Oct. 19, 2012
TOPIC: Featured News, Medical

FDA advisory panel recommends approval of TWO new agents for HoFH

Posted at October 19, 2012 2:54 pm by E. Michael D. (Mike) Scott

In an extraordinary signal of the progress that is being made to find treatments for some types of rare disorders, an advisory committee to the U.S. Food and Drug Administration (FDA) has recommended approval this week for not just one but two new drugs to treat homozygous familial hypercholesterolemia (HoFH).

read more >

TAGS: , , , , , , , ,
Oct. 18, 2012
TOPIC: Advocacy, Featured News, Industry, Medical, Patients & Members, Research

Welcome to our blog!

Posted at October 18, 2012 8:00 am by Peter L Saltonstall

NORD’s Board Chair and President with Senator Hagan

Welcome to NORD’s new blog!  We hope you will visit often and that you will join the conversation. Topics we’ll be covering in upcoming posts include:

read more >

TAGS: , , ,
123

Contact NORD

Featured Partnerships

Translate This page:

SUBSCRIBE TO OUR E-NEWS

EURORDISRare Disease Day USNORD
Copyright ©2012 NORD - National Organization for Rare Disorders, Inc. All rights reserved.
Privacy Statement