Oct. 19, 2012
Posted at October 19, 2012 2:54 pm by E. Michael D. (Mike) Scott

2 Responses to FDA advisory panel recommends approval of TWO new agents for HoFH

  1. Thomas Murphy says:

    Tremendous … I believe we are going to begin seeing similar circumstances with ALS in the near future with Dexpramipexole, NP001, CK-357/Tirasemtiv, Nueralstem and Brainstorm … can you imagine – 5 treatments coming along all at around the same time!

  2. salva says:

    These are great news! Hopefully this sparks new research in other rare diseases.

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