If you’ve never seen or heard NIH Director Francis Collins talking about drug development — and specifically the development of new drugs for rare disorders — just click here to see his TED presentation recorded last year but just posted to the TED.com web site in the past couple of days.
Reprinted with permission from FDA Matters:By Steven Grossman
The Orphan Drug Act (ODA) turned 30 this month, demonstrating that good laws really can have an enduring impact. Amidst the celebrations, a reporter asked me a provocative question: Can we afford more orphan drugs costing hundreds of thousands of dollars per year? FDA Matters answered “yes”. read more >
An article in the January issue of Therapeutic Innovation and Regulatory Science (formerly the Drug Information Journal) offers continuing insights into how the pharmaceutical and biotechnology industries and their regulators need to be thinking about drug development for the future … and these insights are particularly appropriate when it comes to the rare disease space. read more >