Tag: Michael Scott | Rare Disease Dialog Blog

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Mar. 21, 2013

Francis Collins on developing drugs for rare disorders.

Posted at March 21, 2013 7:23 pm by E. Michael D. (Mike) Scott

If you’ve never seen or heard NIH Director Francis Collins talking about drug development — and specifically the development of new drugs for rare disorders — just click here to see his TED presentation recorded last year but just posted to the TED.com web site in the past couple of days.

TAGS: drug development, Francis Collins, Michael Scott, NIH Director

Nov. 02, 2012

TOPIC: Featured News, Industry, Medical, Research

Glybera Becomes First-ever Gene Therapy Approved in Europe

Posted at November 2, 2012 7:37 pm by E. Michael D. (Mike) Scott

According to a report on the BBC News web site today, the European Commission has — for the very first time anywhere in the Western world — given final approval to market a gene therapy that corrects an inborn error of metabolism for the treatment of any type of human genetic disorder. read more >

TAGS: European Commission, Gene therapy, Glybera, Lipoprotein Lipase Deficiency, LPLD, Marketing Approval, Michael Scott

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How do you use online communities? Check out new blog by Allie Freitas- disucsses @RareConnect! #raredisease http://t.co/dREPfjeHIw 02:11:17 PM May 13, 2013
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